Transplant is beneficial earlier in life, Wang told MedPage Today, but carries potential short- and long-term side effects.

The majority of SCD patients given Lyfgenia in clinical trials remained free of vaso-occlusive events (VOEs) following ...

BMS isn’t the only firm trying to use degraders to tackle sickle cell disease. Novartis has a Wiz-targeting glue degrader, ...

The most-read gene therapy articles included topics on FDA approvals, chimeric antigen receptor T-cell therapies, the ...

In the USA, children with sickle cell disease increasingly survive into adulthood, leading to an expanding population of ...

CHICAGO (CBS) -- The Red Cross mission to prevent and relieve human suffering continues even when there's not an emergency, ...

Researchers described a promising new approach for using gene therapy to treat sickle cell disease in the journal Human Gene Therapy. To improve the efficacy of gene therapy when using anti ...

Only one quarter of patients living with sickle cell disease are prescribed disease modifying therapies, particularly newer ...

Learn about sickle cell disease, its impact on the Black community, and the importance of genetic counseling. Know your status.

Sickle cell disease is a condition little understood by most people around the world, despite it being the number one most ...

MTL-HBG is an RNAa medicine designed to increase transcription of the gamma globin gene (HBG), enabling people with sickle cell disease to produce enhanced levels of fetal hemoglobin (HbF).

Nigerian woman opens up about the struggles of living with sickle cell disease, sharing her story to raise genotype ...