UCSF Benioff Children’s Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell ...

Sickle cell disease is a genetic blood disorder caused by a single mutation in both copies of a gene coding for beta-globin. Beta-globin forms half of the oxygen-carrying molecule hemoglobin.

Sickle cell disease occurs when a child inherits two sickle cell genes—one from each parent. Lillian knew she carried the ...

Can the risk of passing on a potentially fatal genetic disease prevent a couple ... a country with a high prevalence of sickle cell disease.

Last May, a 12-year-old with sickle cell anemia was the first person to receive a new gene therapy to treat the disease. The process is painful, expensive, and still frightening and uncertain ...

Sickle cell disease is an inherited genetic condition, explained Dr. Férol Gbénou. It is characterized by abnormal hemoglobin, which can block blood flow and cause pain and organ damage.

Vertex and CRISPR Therapeutics have won the backing of NICE for their gene-editing therapy Casgevy ... a few months after turning it down for sickle cell disease. Final draft guidance published ...

Lawyers for Daniel Penny, who is accused of choking Jordan Neely to death, called an expert who argued that a combination of ...

CRISPR Therapeutics ($CRSP) has endured a tough year since gaining several important regulatory approvals for its ...