In the USA, children with sickle cell disease increasingly survive into adulthood, leading to an expanding population of ...

The majority of SCD patients given Lyfgenia in clinical trials remained free of vaso-occlusive events (VOEs) following ...

BMS isn’t the only firm trying to use degraders to tackle sickle cell disease. Novartis has a Wiz-targeting glue degrader, ...

CHICAGO (CBS) -- The Red Cross mission to prevent and relieve human suffering continues even when there's not an emergency, ...

Learn about sickle cell disease, its impact on the Black community, and the importance of genetic counseling. Know your status.

Transplant is beneficial earlier in life, Wang told MedPage Today, but carries potential short- and long-term side effects.

As he got older, he learned he had sickle cell disease: His red blood cells were forming sickle shapes and getting stuck in his blood stream, preventing oxygen from reaching his tissues.

The most-read gene therapy articles included topics on FDA approvals, chimeric antigen receptor T-cell therapies, the ...

SAN DIEGO — The approval one year ago of two genetic medicines for sickle cell disease, including the first therapy powered by CRISPR gene editing, was a milestone for people living with a ...

MTL-HBG is an RNAa medicine designed to increase transcription of the gamma globin gene (HBG), enabling people with sickle cell disease to produce enhanced levels of fetal hemoglobin (HbF).

(RTTNews) - Beam Therapeutics Inc. (BEAM) announced new safety and efficacy data from its BEACON Phase 1/2 clinical trial of BEAM-101 in patients with sickle cell disease (SCD) with severe vaso ...